A film about some of the challenges in gene therapy, and a promising new approach

Duchenne UK has granted £655,000 to a pre-clinical DMD program with Evox Therapeutics, a company looking at using exosomes to deliver the gene without using a virus.

We are living through exciting times for research into Duchenne Muscular Dystrophy. Several companies are now testing an approach that uses a man-made gene to replace the gene that’s faulty in Duchenne. This is known as gene transfer using micro-dystrophin. Or more commonly, gene therapy.
The early data looks very promising for gene therapy. But challenges do still exist in getting this treatment to the entire Duchenne population. Here we explain what some of these challenges are, and some potential solution, including a new £655,000 project being funded by Duchenne UK.

For more information visit: https://www.duchenneuk.org/news/evox-therapeutics-grant

Видео A film about some of the challenges in gene therapy, and a promising new approach канала Duchenne UK