Genomic Therapeutics: Seeking a Cure for Premature Aging -- The Frank and Joan Rothman Lecture

Hutchinson-Gilford progeria syndrome is the most dramatic form of premature aging, and most cases are caused by a single nucleotide misspelling in the lamin A gene. An intense team effort to identify effective therapies has recently led to the first FDA-approved drug that provides significant benefit. But now greater promise is emerging in adapting RNA morpholino and DNA gene editing therapeutics.

Francis Collins, MD, Acting Science Advisor to President Joe Biden, former Director of the National Institutes of Health

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